Do discussions about gene therapy leave you scratching your head? Well look no further- the following video will guide you through how genes work- as blueprints that determine everything about the body, including how well you clot – and why gene therapy can be used to create new therapies for hemophilia.
‘Jean’ explains how gene therapy works to overcome the mutations in genes, such as the genes that produce clotting factor. Scientists use vectors- viruses that have been emptied of the part that makes people sick- to introduce functional genes into the body. And once these functional genes are reproduced, they start to make effective clotting proteins in cells. Curious to know more? Click here to watch the full NHF video “What is Gene Therapy?”
Have you ever thought about creating an e-book or guest authoring
on other blogs? I have a blog centered on the same
ideas you discuss and would love to have you share some stories/information. I know my visitors would appreciate your work.
If you are even remotely interested, feel free to shoot me an e-mail.
Thank you for your comments. E-books or guest authoring on other blogs isn’t part of our communications plan at this time, but if you would like to send us a link to your blog, we will review and let you know if we ever change our strategy.